CRISPR Therapeutics AG
Biotechnology, Gene Editing, PharmaceuticalLeading gene editing company developing CRISPR-based medicines for serious diseases including sickle cell disease and beta thalassemia.
- Headquarters
- Zug, Switzerland
- Founder
- Emmanuelle Charpentier, Ph.D., Jennifer Doudna, Ph.D.
- Founded
- 2013
- Employees
- 500
- Type
- Public
Expertise: CRISPR/Cas9 gene editing, Hemoglobinopathies, Immuno-Oncology, Autoimmune diseases, In Vivo gene editing, Regenerative Medicine
CRISPR Therapeutics
Biotechnology, Gene Editing, PharmaceuticalCRISPR-based gene editing company developing medicines for serious genetic diseases.
- Headquarters
- Zug, Switzerland
- Founded
- 2014
- Employees
- 900
- Type
- Public
Expertise: CRISPR/Cas9 gene editing, Hemoglobinopathies, In Vivo gene editing, Immuno-Oncology, Regenerative Medicine
Editas Medicine
Biotechnology, Gene Editing, PharmaceuticalGene editing company developing CRISPR-based therapies for genetic and acquired diseases.
- Headquarters
- Cambridge, United States
- Founded
- 2013
- Employees
- 500
- Type
- Public
Expertise: CRISPR/Cas9 gene editing, In Vivo gene editing, Hemoglobinopathies, Immuno-Oncology, Regenerative Medicine
Vertex Pharmaceuticals
Biotechnology, Pharmaceutical, Gene TherapyBiopharmaceutical company developing cell and gene therapies for serious genetic diseases.
- Headquarters
- Boston, United States
- Founded
- 1989
- Employees
- 2,500
- Type
- Public
Expertise: Gene therapy, CRISPR applications, Hemoglobinopathies, Cell therapy, Regenerative Medicine
Sangamo Therapeutics
Biotechnology, Gene Editing, PharmaceuticalGene editing company using zinc finger nucleotide technology for serious genetic diseases.
- Headquarters
- Richmond, United States
- Founded
- 1995
- Employees
- 400
- Type
- Public
Expertise: Zinc finger nucleotides, Gene editing, Hemoglobinopathies, In Vivo gene therapy, Immunology
Beam Therapeutics
Biotechnology, Gene Editing, PharmaceuticalBase editing gene therapy company treating genetic diseases with precision editing technology.
- Headquarters
- Cambridge, United States
- Founded
- 2017
- Employees
- 400
- Type
- Public
Expertise: Base editing, Gene editing, Hemoglobinopathies, In Vivo gene therapy, Immuno-Oncology
Bluebird Bio
BiotechnologyGene therapy company focused on rare blood disorders and severe genetic diseases.
- Headquarters
- Cambridge, United States
- Founded
- 1992
- Employees
- 800
- Type
- Public
Expertise: Gene therapy, cell therapy, lentiviral vectors, blood disorders
Intellia Therapeutics
BiotechnologyCRISPR-based gene editing company developing in vivo therapies for serious genetic diseases.
- Headquarters
- Cambridge, United States
- Founded
- 2014
- Employees
- 250
- Type
- Public
Expertise: CRISPR gene editing, in vivo therapeutics, genetic disorders, oncology
Exonics Therapeutics
BiotechnologyRNA therapeutics company developing exon-skipping treatments for muscular dystrophy and rare genetic diseases.
- Headquarters
- Philadelphia, United States
- Founded
- 2017
- Type
- Private
Expertise: Exon-skipping technology, genetic disorders, RNA therapeutics, muscular dystrophy
Translate Bio
BiotechnologyDevelops mRNA therapeutics for genetic and rare diseases, acquired by Sanofi.
- Headquarters
- Lexington, USA
- Founded
- 2011
- Type
- Subsidiary
Expertise: mRNA therapeutics, Genetic medicine, Rare diseases, Protein replacement
Excision BioTherapeutics
BiotechnologyDevelops CRISPR-based therapies targeting chronic viral infections like herpes and HIV.
- Headquarters
- Dallas, USA
- Founded
- 2016
- Type
- Private
Expertise: Gene editing, Chronic viral infections, CRISPR-Cas, Herpes therapy
Homology Medicines
BiotechnologyDevelops proprietary gene therapy platform for monogenic and metabolic diseases.
- Headquarters
- Bedford, USA
- Founded
- 2015
- Employees
- 75
- Type
- Private
Expertise: Gene therapy, Gene editing, Metabolic diseases, Genetic disorders