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Companies similar to gene editing companies

12 competitors and alternatives to gene editing companies — out of roughly 287 similar companies worldwide. Data is AI-generated and may be approximate.

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CRISPR Therapeutics AG

Biotechnology, Gene Editing, Pharmaceutical

Leading gene editing company developing CRISPR-based medicines for serious diseases including sickle cell disease and beta thalassemia.

Headquarters
Zug, Switzerland
Founder
Emmanuelle Charpentier, Ph.D., Jennifer Doudna, Ph.D.
Founded
2013
Employees
500
Type
Public

Expertise: CRISPR/Cas9 gene editing, Hemoglobinopathies, Immuno-Oncology, Autoimmune diseases, In Vivo gene editing, Regenerative Medicine

CRISPR Therapeutics

Biotechnology, Gene Editing, Pharmaceutical

CRISPR-based gene editing company developing medicines for serious genetic diseases.

Headquarters
Zug, Switzerland
Founded
2014
Employees
900
Type
Public

Expertise: CRISPR/Cas9 gene editing, Hemoglobinopathies, In Vivo gene editing, Immuno-Oncology, Regenerative Medicine

Editas Medicine

Biotechnology, Gene Editing, Pharmaceutical

Gene editing company developing CRISPR-based therapies for genetic and acquired diseases.

Headquarters
Cambridge, United States
Founded
2013
Employees
500
Type
Public

Expertise: CRISPR/Cas9 gene editing, In Vivo gene editing, Hemoglobinopathies, Immuno-Oncology, Regenerative Medicine

Vertex Pharmaceuticals

Biotechnology, Pharmaceutical, Gene Therapy

Biopharmaceutical company developing cell and gene therapies for serious genetic diseases.

Website
vrtx.com
Headquarters
Boston, United States
Founded
1989
Employees
2,500
Type
Public

Expertise: Gene therapy, CRISPR applications, Hemoglobinopathies, Cell therapy, Regenerative Medicine

Sangamo Therapeutics

Biotechnology, Gene Editing, Pharmaceutical

Gene editing company using zinc finger nucleotide technology for serious genetic diseases.

Headquarters
Richmond, United States
Founded
1995
Employees
400
Type
Public

Expertise: Zinc finger nucleotides, Gene editing, Hemoglobinopathies, In Vivo gene therapy, Immunology

Beam Therapeutics

Biotechnology, Gene Editing, Pharmaceutical

Base editing gene therapy company treating genetic diseases with precision editing technology.

Website
beamtx.com
Headquarters
Cambridge, United States
Founded
2017
Employees
400
Type
Public

Expertise: Base editing, Gene editing, Hemoglobinopathies, In Vivo gene therapy, Immuno-Oncology

Bluebird Bio

Biotechnology

Gene therapy company focused on rare blood disorders and severe genetic diseases.

Headquarters
Cambridge, United States
Founded
1992
Employees
800
Type
Public

Expertise: Gene therapy, cell therapy, lentiviral vectors, blood disorders

Intellia Therapeutics

Biotechnology

CRISPR-based gene editing company developing in vivo therapies for serious genetic diseases.

Headquarters
Cambridge, United States
Founded
2014
Employees
250
Type
Public

Expertise: CRISPR gene editing, in vivo therapeutics, genetic disorders, oncology

Exonics Therapeutics

Biotechnology

RNA therapeutics company developing exon-skipping treatments for muscular dystrophy and rare genetic diseases.

Headquarters
Philadelphia, United States
Founded
2017
Type
Private

Expertise: Exon-skipping technology, genetic disorders, RNA therapeutics, muscular dystrophy

Translate Bio

Biotechnology

Develops mRNA therapeutics for genetic and rare diseases, acquired by Sanofi.

Headquarters
Lexington, USA
Founded
2011
Type
Subsidiary

Expertise: mRNA therapeutics, Genetic medicine, Rare diseases, Protein replacement

Excision BioTherapeutics

Biotechnology

Develops CRISPR-based therapies targeting chronic viral infections like herpes and HIV.

Headquarters
Dallas, USA
Founded
2016
Type
Private

Expertise: Gene editing, Chronic viral infections, CRISPR-Cas, Herpes therapy

Homology Medicines

Biotechnology

Develops proprietary gene therapy platform for monogenic and metabolic diseases.

Headquarters
Bedford, USA
Founded
2015
Employees
75
Type
Private

Expertise: Gene therapy, Gene editing, Metabolic diseases, Genetic disorders

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